Search Results
E. Buratti - RNA splicing therapy in Pompe disease
E. Buratti - New RNA-based therapeutic strategies for Glycogenosis Type 2 (Pompe disease)
E. Buratti - RNA splicing mutations and human disease
E. Buratti - Molecular pathology of pre-mRNA splicing (Part 1)
E. Buratti - Aberrant RNA processing in neurodegeneration - RNA Structure and Function 2016
35. Gene Therapy for Pompe Disease: From Bench to Bedside with Dr. Giuseppe Ronzitti
2021 Conference Dr Barry Byrne - Gene Therapy
E. Buratti - Molecular mechanisms in neurodegeneration
Bioethics Emanuele Buratti, Molecular Pathology ICGEB Trieste
2nd Tier Molecular Testing for Pompe disease and MPSI
34. Lentiviral Gene Therapy and Antisense Oligonucleotides for Pompe Disease with Dr. Pim Pijnappel
L. Carrier - RNA-based therapy for cardiac genetic disease