Search Results
E. Buratti - RNA splicing therapy in Pompe disease
E. Buratti - New RNA-based therapeutic strategies for Glycogenosis Type 2 (Pompe disease)
E. Buratti - RNA splicing mutations and human disease
E. Buratti - Molecular pathology of pre-mRNA splicing (Part 1)
E. Buratti - Aberrant RNA processing in neurodegeneration - RNA Structure and Function 2016
35. Gene Therapy for Pompe Disease: From Bench to Bedside with Dr. Giuseppe Ronzitti
2021 Conference Dr Barry Byrne - Gene Therapy
34. Lentiviral Gene Therapy and Antisense Oligonucleotides for Pompe Disease with Dr. Pim Pijnappel
E. Buratti - Molecular mechanisms in neurodegeneration
Bioethics Emanuele Buratti, Molecular Pathology ICGEB Trieste
2nd Tier Molecular Testing for Pompe disease and MPSI
L. Carrier - RNA-based therapy for cardiac genetic disease
