Search Results
E. Buratti - RNA splicing therapy in Pompe disease
E. Buratti - New RNA-based therapeutic strategies for Glycogenosis Type 2 (Pompe disease)
E. Buratti - RNA splicing mutations and human disease
E. Buratti - Molecular pathology of pre-mRNA splicing (Part 1)
E. Buratti - Aberrant RNA processing in neurodegeneration - RNA Structure and Function 2016
E. Buratti - Molecular mechanisms in neurodegeneration
34. Lentiviral Gene Therapy and Antisense Oligonucleotides for Pompe Disease with Dr. Pim Pijnappel
2nd Tier Molecular Testing for Pompe disease and MPSI
PREVIEW: Battling Pompe Disease
Pompe disease-Coping with Isolation and loneliness
35. Gene Therapy for Pompe Disease: From Bench to Bedside with Dr. Giuseppe Ronzitti
2021 Conference Dr Barry Byrne - Gene Therapy